Neurogene reports rapid MECP2 expression and new gene regulation data for NGN-401 in Rett syndrome
Neurogene reports rapid MECP2 expression and new regulation data for NGN-401, strengthening its Rett syndrome research ahead of 2027 results.
Neurogene reports rapid MECP2 expression and new regulation data for NGN-401, strengthening its Rett syndrome research ahead of 2027 results.
Eloxx starts Phase 2b testing of exaluren in nonsense mutation Alport syndrome, with a 16-week biomarker readout expected in mid-2027.