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Representative image: Oral preventive therapy for hereditary angioedema as BioCryst Pharmaceuticals expands ORLADEYO into younger children in Japan, strengthening the drug’s global pediatric HAE growth opportunity.

Pharma & Biotech

Japan approves pediatric ORLADEYO as BioCryst Pharmaceuticals expands hereditary angioedema reach

by Soujanya Ravi
August 25, 2026
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Japan expands ORLADEYO to children aged 2 to under 12 as BioCryst Pharmaceuticals builds its global HAE franchise. See what comes next.

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Pharma & Biotech

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Representative image of biopharma laboratory research. Gilead Sciences and Merck’s latest Phase 3 updates highlight the promise of once-weekly HIV treatment with islatravir and lenacapavir, while raising fresh questions over Trodelvy’s lung cancer expansion strategy.

Pharma & Biotech

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clinical trials Eli Lilly and Company European Medicines Agency FDA FDA approval immuno-oncology immunotherapy Inc. Johnson & Johnson medical devices oncology precision oncology U.S. Food and Drug Administration United States Food and Drug Administration US Food and Drug Administration

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