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pediatric hematology

PharmaDeviceNews pediatric hematology

Representative image: Vertex Pharmaceuticals’ expanded FDA approval for CASGEVY opens CRISPR gene therapy to children aged 2 and older with sickle cell disease and transfusion-dependent beta thalassemia.

Pharma & Biotech

Vertex expands CASGEVY to young children with sickle cell disease and beta thalassemia

by Pallavi Madhiraju
July 2, 2026
0 Comments

Explore how the FDA’s CASGEVY age expansion could reshape early gene therapy for sickle cell disease and beta thalassemia. Read more.

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