Why Aurora Therapeutics believes the FDA is ready for grouped CRISPR approvals
Can Aurora Therapeutics make CRISPR work at scale? Find out how its platform model for rare disease editing is testing biotech’s next big leap.
PTC Therapeutics receives Japanese approval for Sephience in full-spectrum PKU
Japan approves Sephience for PKU across all ages. Find out what this means for PTC Therapeutics’ global rare disease expansion strategy.