FDA fast track for Argo Biopharma’s BW-20805 siRNA puts HAE’s next competitive battleground in focus

FDA fast track for Argo Biopharma’s BW-20805 siRNA puts HAE’s next competitive battleground in focus

Argo Biopharmaceutical Co., Ltd. (Argo Biopharma), a Shanghai-based clinical-stage RNA interference therapeutics company, has received Fast Track Designation from the U.S. Food and Drug Administration for BW-20805, its investigational small interfering RNA therapy targeting prekallikrein for the prevention of hereditary angioedema attacks. The designation comes as the company runs a global Phase II open-label study […]

Sentynl Therapeutics licenses Progerinin for progeria as rare-disease strategy expands beyond Zokinvy

Sentynl Therapeutics licenses Progerinin for progeria as rare-disease strategy expands beyond Zokinvy

Sentynl Therapeutics Inc., the United States-based rare disease subsidiary of Zydus Lifesciences Limited, has entered into a licensing agreement with South Korean biotechnology company PRG S&T to develop the investigational molecule Progerinin (SLC-D011) for Hutchinson-Gilford Progeria Syndrome, an ultra-rare genetic disorder that causes accelerated aging in children. The therapy has received orphan drug designation from […]

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